DrugEvidence

Drugs / Everolimus

Everolimus

Drug

Marketed as Afinitor

Everolimus is an mTOR-targeted medicine marketed as Afinitor and used in oncology and other indications. It is used as targeted therapy in renal cell cancer and other tumors, and it is also used as an immunosuppressant in transplant settings. The drug has multiple U.S. FDA approvals across indications.

Trials
795
Recruiting
49
Completed
465
With results
305

Last revised

Pipeline

Phase by status

PhaseRecruitingNot yetBy invitationActiveCompletedTerminatedWithdrawnSuspendedUnknownNo longer availableTotal
Early Phase 1 342 9
Phase 1 51101012237 149
Phase 1/2 52126514118 99
Phase 2 23416156549235 299
Phase 2/3 2111312 11
Phase 3 621063828 99
Phase 4 1212588215 89
Not applicable 2110327 25
Unknown 2715 15

Trials started per year

2021
6
2022
15
2023
15
2024
17
2025
15
2026
16

Conditions studied, by phase

ConditionEarly Phase 1Phase 1Phase 1/2Phase 2Phase 2/3Phase 3Phase 4Not applicableUnknownTotal
Breast Neoplasms 20134918214 107
Carcinoma, Renal Cell 1176307532 71
Neoplasm Metastasis 1155181314 48
Neoplasms 10315233 36
Neuroendocrine Tumors 102111632 35
Kidney Neoplasms 531432 27
Recurrence 183511 19
Tuberous Sclerosis 155232 18
Carcinoma, Non-Small-Cell Lung 1322 17
Lymphoma 52611 15

Most active sponsors

#SponsorTrialsPhase 3
1Novartis Pharmaceuticals13443
2M.D. Anderson Cancer Center350
3Dana-Farber Cancer Institute190
4Memorial Sloan Kettering Cancer Center160
5Emory University130
6Fudan University112
7National Cancer Institute (NCI)111
8Mayo Clinic100
9SCRI Development Innovations, LLC100
10Alliance for Clinical Trials in Oncology81

Most studied interventions

#InterventionTrials
1Everolimus795
2Mycophenolic Acid74
3Tacrolimus61
4Cyclosporine41
5Bevacizumab37
6exemestane37
7Sorafenib32
8Sirolimus31
9Letrozole26
10Paclitaxel25

Evidence

Results reported
65.6%305 of 465 completed
Published
15.3%71 of 465 completed
Primary endpoint met
40.9%36 of 88 analyses
Median months to report
12

Documents disclosed

Protocol available
122
Statistical analysis plan
121
PubMed citations
99

Trial profile

Median enrollment
44
Median duration
52.9months
Countries
68
Study sites
7852

Who is enrolled

Adults
785
Children
75
Older adults
747
Healthy volunteers
15

Median enrollment by phase

Early Phase 1
8
Phase 1
27
Phase 1/2
40
Phase 2
43
Phase 2/3
60
Phase 3
256
Phase 4
71
Not applicable
36
Unknown
99

Where trials run

United States
432
Germany
117
France
115
Italy
94
Spain
87
United Kingdom
69
South Korea
63
Netherlands
62
Belgium
56
Canada
53

Busiest cities

#CityCountryTrials
1HoustonUnited States116
2BostonUnited States105
3New YorkUnited States104
4Los AngelesUnited States77
5BarcelonaSpain75
6BerlinGermany69
7NashvilleUnited States67
8MilanItaly65
9MadridSpain64
10PhiladelphiaUnited States62

Terminations

Terminated
114
Withdrawn
20
Suspended
3
Stopped for recruitment
6.3%50 of 795 trials

Stated reasons

Other / unclear
52
Recruitment
50
Funding
11
Safety
10
Business decision
7
Lack of efficacy
6
Regulatory
1

Reasons are grouped from the sponsor's own wording with a rule-based classifier; the original text is shown below.

Recently stopped

TrialStatusStated reasonStopped
NCT04118556 Terminated Terminated Too slow recruitment 2026-04-29
NCT03065387 Terminated Terminated \<75% participation 2026-04-23
NCT04895748 Terminated Terminated Business decision and not related to safety concerns 2026-02-13
NCT03632317 Withdrawn Withdrawn low accrual 2025-10-31
NCT02860494 Withdrawn Withdrawn Pharmaceutical and financial difficulties 2024-12-31
NCT04305444 Terminated Terminated Despite the efforts of our dedicated team and initial progress, we were unable to secure the necessary financial resources to continue the study. We appreciate the support and participation of all involved. 2024-12-31
NCT03284957 Terminated Terminated Sponsor decision to prematurely stop the study, not linked to any safety concern. 2024-11-08
NCT05079360 Withdrawn Withdrawn Decided to halt and will potentially reopen in the future. 2024-05-26
NCT01345136 Terminated Terminated slow accrual 2024-02-06
NCT05065411 Terminated Terminated Business decision 2024-01-09

Trial records