DrugEvidence

Diseases / Cholangiocarcinoma

Cholangiocarcinoma

Disease

Cholangiocarcinoma is bile duct cancer, an adenocarcinoma arising from the biliary epithelium that can occur intrahepatically or extrahepatically. It is often diagnosed at advanced stages and generally has poor prognosis.

Trials
770
Recruiting
155
Completed
223
With results
96

Last revised

Pipeline

Phase by status

PhaseRecruitingNot yetBy invitationActiveCompletedTerminatedWithdrawnSuspendedUnknownApproved for marketingAvailableNo longer availableTotal
Early Phase 1 2112 6
Phase 1 183123623519 107
Phase 1/2 1021517127 54
Phase 2 5018223863012137 259
Phase 2/3 42425 17
Phase 3 53478110 38
Phase 4 1214 8
Not applicable 2610152913528 117
Unknown 39163445106134222 164

Trials started per year

2021
10
2022
60
2023
55
2024
89
2025
55
2026
55
2027
2

Conditions studied, by phase

ConditionEarly Phase 1Phase 1Phase 1/2Phase 2Phase 2/3Phase 3Phase 4Not applicableUnknownTotal
Cholangiocarcinoma 61075425917388117164 770
Pancreatic Neoplasms 131815122441 123
Carcinoma, Hepatocellular 18521222343 114
Gallbladder Neoplasms 148482111718 109
Biliary Tract Neoplasms 11104048618 97
Colorectal Neoplasms 3491711915 86
Liver Neoplasms 13512111032 74
Stomach Neoplasms 12911101516 73
Bile Duct Neoplasms 962626616 71
Ovarian Neoplasms 12378129 51

Most active sponsors

#SponsorTrialsPhase 3
1National Cancer Institute (NCI)220
2Shanghai Zhongshan Hospital162
3Mayo Clinic140
4Fudan University121
5Tianjin Medical University Cancer Institute and Hospital111
6M.D. Anderson Cancer Center100
7Institut für Klinische Krebsforschung IKF GmbH at Krankenhaus Nordwest90
8Peking Union Medical College Hospital80
9Sun Yat-sen University80
10Washington University School of Medicine80

Most studied interventions

#InterventionTrials
1Gemcitabine118
2Cisplatin82
3Oxaliplatin46
4pembrolizumab37
5Capecitabine33
6Fluorouracil33
7durvalumab30
8lenvatinib28
9Leucovorin27
10Magnetic Resonance Spectroscopy18

Evidence

Results reported
43%96 of 223 completed
Published
16.1%36 of 223 completed
Primary endpoint met
46.7%7 of 15 analyses
Median months to report
12

Documents disclosed

Protocol available
77
Statistical analysis plan
76
PubMed citations
181

Trial profile

Median enrollment
57
Median duration
40.7months
Countries
58
Study sites
5502

Who is enrolled

Adults
768
Children
38
Older adults
767
Healthy volunteers
29

Median enrollment by phase

Early Phase 1
10
Phase 1
38
Phase 1/2
72
Phase 2
40
Phase 2/3
150
Phase 3
188
Phase 4
47
Not applicable
60
Unknown
168

Where trials run

United States
311
China
203
France
68
South Korea
65
Germany
59
Italy
55
Spain
49
United Kingdom
42
Canada
41
Australia
36

Busiest cities

#CityCountryTrials
1HoustonUnited States98
2New YorkUnited States88
3ShanghaiChina63
4SeoulSouth Korea60
5BostonUnited States59
6Los AngelesUnited States53
7ChicagoUnited States52
8RochesterUnited States49
9DallasUnited States48
10NashvilleUnited States47

Terminations

Terminated
98
Withdrawn
32
Suspended
3
Stopped for recruitment
4.4%34 of 770 trials

Stated reasons

Other / unclear
54
Recruitment
34
Business decision
16
Funding
10
Regulatory
8
Lack of efficacy
5
COVID-19
4
Safety
2

Reasons are grouped from the sponsor's own wording with a rule-based classifier; the original text is shown below.

Recently stopped

TrialStatusStated reasonStopped
NCT04985357 Withdrawn Withdrawn Abandoned prior to launch. 2030-05-31
NCT05514912 Withdrawn Withdrawn PI has decided to terminate this study due to study supporter pulling support on this study. 2027-06-23
NCT06572189 Withdrawn Withdrawn Based on the results of another intravenous injection therapy CD-801 for the treatment of hepatocellular carcinoma, we have decided to change the administration method and therefore withdraw this trial protocol. 2026-07-31
NCT02626312 Terminated Terminated \< 75% participation 2026-06-10
NCT05712356 Terminated Terminated The study was halted prematurely to allow analysis of the results. 2026-04-05
NCT05325866 Terminated Terminated Sponsor Decision 2026-01-28
NCT05346484 Terminated Terminated Portfolio prioritization 2026-01-12
NCT02917759 Terminated Terminated Lack of funding to support enrollment 2025-12-31
NCT06284226 Withdrawn Withdrawn The project is terminated 2025-12-31
NCT05275478 Terminated Terminated Sponsor Decision - Business Decisions 2025-12-30

Trial records