DrugEvidence

Diseases / Pulmonary Arterial Hypertension

Pulmonary Arterial Hypertension

Disease

Pulmonary arterial hypertension is a progressive pulmonary vascular disease characterized by elevated pulmonary arterial pressure and vascular remodeling, which can lead to right ventricular failure.

Trials
690
Recruiting
76
Completed
339
With results
171

Last revised

Pipeline

Phase by status

PhaseRecruitingNot yetBy invitationActiveCompletedTerminatedWithdrawnUnknownAvailableNo longer availableTotal
Early Phase 1 1211 5
Phase 1 4352641 70
Phase 1/2 316112 14
Phase 2 1273582565 116
Phase 2/3 12411 9
Phase 3 10214562182 104
Phase 4 432281466 63
Not applicable 13165474729 121
Unknown 281235861053315 188

Trials started per year

2021
11
2022
28
2023
37
2024
31
2025
31
2026
52
2027
2

Conditions studied, by phase

ConditionEarly Phase 1Phase 1Phase 1/2Phase 2Phase 2/3Phase 3Phase 4Not applicableUnknownTotal
Pulmonary Arterial Hypertension 57014116910463121188 690
Hypertension, Pulmonary 1938231143258 185
Familial Primary Pulmonary Hypertension 2195159 32
Heart Failure 112338 18
Lung Diseases, Interstitial 51237 18
Lung Diseases 341314 16
Cardiovascular Diseases 231513 15
Heart Defects, Congenital 1185 15
Hypertension 375 15
Connective Tissue Diseases 145111 13

Most active sponsors

#SponsorTrialsPhase 3
1Actelion5930
2United Therapeutics4414
3Bayer193
4Pfizer's Upjohn has merged with Mylan to form Viatris Inc.133
5Bial - Portela C S.A.120
6Merck Sharp & Dohme LLC123
7Novartis Pharmaceuticals126
8Assistance Publique - Hôpitaux de Paris102
9Pfizer104
10University of Sao Paulo General Hospital100

Most studied interventions

#InterventionTrials
1treprostinil43
2Sildenafil Citrate34
3Bosentan29
4ambrisentan24
5Iloprost21
6macitentan21
7ACE-01117
8Tadalafil17
9selexipag15
10riociguat12

Evidence

Results reported
50.4%171 of 339 completed
Published
13%44 of 339 completed
Primary endpoint met
46.2%48 of 104 analyses
Median months to report
13

Documents disclosed

Protocol available
82
Statistical analysis plan
81
PubMed citations
151

Trial profile

Median enrollment
44
Median duration
31months
Countries
67
Study sites
5609

Who is enrolled

Adults
668
Children
131
Older adults
606
Healthy volunteers
98

Median enrollment by phase

Early Phase 1
10
Phase 1
25
Phase 1/2
24
Phase 2
31
Phase 2/3
90
Phase 3
156
Phase 4
30
Not applicable
40
Unknown
100

Where trials run

United States
309
Germany
119
France
102
United Kingdom
98
Canada
85
Italy
76
Spain
76
China
73
Australia
67
Belgium
65

Busiest cities

#CityCountryTrials
1BostonUnited States112
2DallasUnited States97
3PittsburghUnited States92
4New YorkUnited States90
5HoustonUnited States89
6Los AngelesUnited States88
7CincinnatiUnited States78
8AuroraUnited States72
9LondonUnited Kingdom72
10RochesterUnited States70

Terminations

Terminated
83
Withdrawn
37
Stopped for recruitment
4.3%30 of 690 trials

Stated reasons

Other / unclear
49
Recruitment
30
Business decision
16
Safety
9
COVID-19
6
Regulatory
6
Lack of efficacy
3
Funding
1

Reasons are grouped from the sponsor's own wording with a rule-based classifier; the original text is shown below.

Recently stopped

TrialStatusStated reasonStopped
NCT06643143 Withdrawn Withdrawn Study has undergone sponsorship and design changes. 2027-06-30
NCT04254289 Withdrawn Withdrawn Lack of enrollment 2025-12-31
NCT04954742 Terminated Terminated Strategic re-prioritization by the IMP supplier. Decision not safety-related 2025-08-13
NCT04811092 Terminated Terminated Study was stopped early due to loss of clinical equipoise based on robust evidence of clinical benefit of sotatercept demonstrated in previous studies. 2025-04-03
NCT06493461 Terminated Terminated Sponsor's Decision 2025-03-31
NCT05975905 Terminated Terminated The study was voluntarily terminated early, following a safety review and observation of pericardial effusions. 2025-03-11
NCT05060315 Terminated Terminated Sponsor Decision 2024-12-31
NCT03782818 Terminated Terminated The recruitment was stopped on October 31st 2024 due to limited recruitment within the last year, as well as the end of funding (Spring 2025). 2024-10-31
NCT02525926 Terminated Terminated Refusal of CPP to extend the period of inclusion 2024-10-17
NCT05036135 Terminated Terminated The IMPAHCT study demonstrated that while inhaled imatinib was well tolerated, it did not prove to be efficacious at any of the doses of AV-101 evaluated in the study. 2024-08-09

Trial records