DrugEvidence

Diseases / Thrombocytopenia

Thrombocytopenia

Disease

Thrombocytopenia is a condition characterized by a lower-than-normal platelet count, increasing risk of bruising and bleeding. Causes include decreased production, increased destruction, splenic sequestration, medications, infections, and systemic disease.

Trials
406
Recruiting
35
Completed
211
With results
103

Last revised

Pipeline

Phase by status

PhaseRecruitingNot yetBy invitationActiveCompletedTerminatedWithdrawnUnknownAvailableNo longer availableTotal
Early Phase 1 1122 6
Phase 1 220211 26
Phase 1/2 1111262 23
Phase 2 14315421617 116
Phase 2/3 111336 15
Phase 3 2133107 53
Phase 4 39518 26
Not applicable 64119333 39
Unknown 532459412211 102

Trials started per year

2021
4
2022
17
2023
23
2024
15
2025
28
2026
13

Conditions studied, by phase

ConditionEarly Phase 1Phase 1Phase 1/2Phase 2Phase 2/3Phase 3Phase 4Not applicableUnknownTotal
Thrombocytopenia 6262311615532639102 406
Purpura, Thrombocytopenic, Idiopathic 141024525 51
Anemia 146121258 39
Neutropenia 341246 29
Hematologic Diseases 261737 26
Hemorrhage 316610 26
Myelodysplastic Syndromes 1321111123 25
Anemia, Aplastic 1121113 19
Jacobs syndrome 125611 16
Autoimmune Diseases 22811 14

Most active sponsors

#SponsorTrialsPhase 3
1GlaxoSmithKline204
2Amgen198
3National Heart, Lung, and Blood Institute (NHLBI)140
4M.D. Anderson Cancer Center103
5Shandong University94
6Novartis Pharmaceuticals72
7Peking University People's Hospital62
8Eisai Inc.52
9Institute of Hematology & Blood Diseases Hospital, China50
10Memorial Sloan Kettering Cancer Center50

Most studied interventions

#InterventionTrials
1eltrombopag60
2romiplostim34
3avatrombopag25
4Platelet Transfusion11
5Thrombopoietin11
6Blood Specimen Collection9
7Cyclosporine7
8Rituximab7
9Cytarabine6
10Dexamethasone6

Evidence

Results reported
48.8%103 of 211 completed
Published
12.3%26 of 211 completed
Primary endpoint met
53.1%26 of 49 analyses
Median months to report
13.5

Documents disclosed

Protocol available
43
Statistical analysis plan
38
PubMed citations
152

Trial profile

Median enrollment
60
Median duration
28.6months
Countries
68
Study sites
2879

Who is enrolled

Adults
389
Children
102
Older adults
357
Healthy volunteers
31

Median enrollment by phase

Early Phase 1
11
Phase 1
25
Phase 1/2
33
Phase 2
35
Phase 2/3
118
Phase 3
130
Phase 4
53
Not applicable
107
Unknown
106

Where trials run

United States
165
China
80
France
46
Italy
35
Canada
32
Germany
30
United Kingdom
23
Spain
22
Australia
21
Russia
21

Busiest cities

#CityCountryTrials
1New YorkUnited States35
2BostonUnited States34
3HoustonUnited States32
4Los AngelesUnited States28
5PhiladelphiaUnited States25
6SeattleUnited States25
7BeijingChina24
8BethesdaUnited States24
9MilanItaly22
10ParisFrance22

Terminations

Terminated
54
Withdrawn
14
Stopped for recruitment
7.6%31 of 406 trials

Stated reasons

Recruitment
31
Other / unclear
20
Business decision
4
Lack of efficacy
4
COVID-19
3
Funding
3
Safety
3

Reasons are grouped from the sponsor's own wording with a rule-based classifier; the original text is shown below.

Recently stopped

TrialStatusStated reasonStopped
NCT06291415 Withdrawn Withdrawn Sponsor decision 2026-11-30
NCT07025512 Withdrawn Withdrawn PI requested 2026-05-04
NCT05785819 Terminated Terminated Veralox Therapeutics Business Decision. 2025-11-17
NCT05040776 Withdrawn Withdrawn Sponsor decision 2025-05-31
NCT04861181 Terminated Terminated End of inclusion period. 2025-04-17
NCT03891576 Terminated Terminated Low accrual rate 2024-08-31
NCT04931849 Withdrawn Withdrawn PI and Sponsor decided to not proceed with the trial. 2024-07-18
NCT03059030 Terminated Terminated Low enrollment 2024-04-04
NCT05091684 Terminated Terminated Only one patient was included in this study due to overly restrictive inclusion and exclusion criteria. 2023-06-27
NCT04889326 Withdrawn Withdrawn COVID 2023-05-01

Trial records