DrugEvidence

Drugs / Cytarabine

Cytarabine

Drug

Cytarabine (cytosine arabinoside, ara-C) is an antimetabolite nucleoside-analog chemotherapy used in leukemias and lymphomas. It is administered via injectable routes, including intravenous and intrathecal use. It is a long-standing oncology medicine and is listed as prescription-only.

Trials
1243
Recruiting
147
Completed
618
With results
352

Last revised

Pipeline

Phase by status

PhaseRecruitingNot yetBy invitationActiveCompletedTerminatedWithdrawnSuspendedUnknownNo longer availableTotal
Early Phase 1 131 5
Phase 1 1911611434178 209
Phase 1/2 173111762859 150
Phase 2 661435258552363 514
Phase 2/3 821696 32
Phase 3 214123113153145 226
Phase 4 2124112 40
Not applicable 1021195318 58
Unknown 31221 9

Trials started per year

2021
6
2022
40
2023
32
2024
55
2025
43
2026
36
2027
2

Conditions studied, by phase

ConditionEarly Phase 1Phase 1Phase 1/2Phase 2Phase 2/3Phase 3Phase 4Not applicableUnknownTotal
Leukemia, Myeloid, Acute 314782198129211203 568
Leukemia 4933110868392 282
Precursor Cell Lymphoblastic Leukemia-Lymphoma 46258611361984 235
Lymphoma 1176906261121 160
Myelodysplastic Syndromes 262552312131 123
Burkitt Lymphoma 12953213211 93
Congenital Abnormalities 131122611431 89
Lymphoma, Non-Hodgkin 12946110151 85
Leukemia, Monocytic, Acute 12372921831 84
Leukemia, Myelomonocytic, Acute 12263011831 82

Most active sponsors

#SponsorTrialsPhase 3
1M.D. Anderson Cancer Center1033
2National Cancer Institute (NCI)8620
3Children's Oncology Group6033
4St. Jude Children's Research Hospital367
5Institute of Hematology & Blood Diseases Hospital, China347
6Fred Hutchinson Cancer Center280
7PETHEMA Foundation251
8Memorial Sloan Kettering Cancer Center222
9European Organisation for Research and Treatment of Cancer - EORTC1610
10SWOG Cancer Research Network161

Most studied interventions

#InterventionTrials
1Cytarabine1243
2Methotrexate352
3Cyclophosphamide348
4Etoposide344
5Daunorubicin301
6Vincristine293
7Dexamethasone258
8Doxorubicin197
9Idarubicin192
10Filgrastim183

Evidence

Results reported
57%352 of 618 completed
Published
21%130 of 618 completed
Primary endpoint met
40.8%31 of 76 analyses
Median months to report
13

Documents disclosed

Protocol available
175
Statistical analysis plan
175
PubMed citations
380

Trial profile

Median enrollment
53
Median duration
67months
Countries
63
Study sites
10096

Who is enrolled

Adults
1190
Children
463
Older adults
846
Healthy volunteers
6

Median enrollment by phase

Early Phase 1
26
Phase 1
21
Phase 1/2
40
Phase 2
50
Phase 2/3
200
Phase 3
355
Phase 4
100
Not applicable
54
Unknown
150

Where trials run

United States
767
China
153
Germany
130
Canada
127
France
98
Australia
95
Italy
89
Spain
83
United Kingdom
69
Belgium
58

Busiest cities

#CityCountryTrials
1HoustonUnited States260
2New YorkUnited States217
3ChicagoUnited States198
4BostonUnited States173
5SeattleUnited States160
6Los AngelesUnited States153
7ColumbusUnited States144
8BaltimoreUnited States140
9ClevelandUnited States137
10St LouisUnited States131

Terminations

Terminated
138
Withdrawn
52
Suspended
1
Stopped for recruitment
4.1%51 of 1243 trials

Stated reasons

Other / unclear
98
Recruitment
51
Funding
16
Business decision
8
Safety
8
Lack of efficacy
6
COVID-19
2
Regulatory
2

Reasons are grouped from the sponsor's own wording with a rule-based classifier; the original text is shown below.

Recently stopped

TrialStatusStated reasonStopped
NCT06692452 Withdrawn Withdrawn Ipsen requested a temporary closure due to a safety concern. 2032-10-01
NCT05330377 Withdrawn Withdrawn Sponsor withdrew funding 2032-05-30
NCT05766514 Withdrawn Withdrawn Study disapproved by internal scientific review committee on re-review; study will no longer move forward 2030-12-31
NCT05521087 Withdrawn Withdrawn Business Decision 2030-01-29
NCT05829434 Withdrawn Withdrawn Trial was stopped prematurely due to safety reasons 2029-08-30
NCT04845035 Withdrawn Withdrawn The PI plans to revise the study design in a new protocol 2029-01-31
NCT07498465 Withdrawn Withdrawn Other - Protocol moved to Withdrawn 2028-11-12
NCT04354025 Withdrawn Withdrawn Principal investigator decided not to move forward with the study. 2028-07-31
NCT05228249 Withdrawn Withdrawn PI left institution and funding sponsor closed study. Study did not open to accrual, and no participants were enrolled. 2027-10-01
NCT06007911 Withdrawn Withdrawn Sponsor withdrew support. 2027-04-30

Trial records